News

Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression.
Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.
After a busy year, columnist Betty Vertin is grateful that her three sons with DMD always have one another for socializing.
The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...
The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...
A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...
Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.
Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation.